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1.?Jett K, Friedman JM. Clinical and genetic aspects of neurofibromatosis 1. Genet Med 2010;?12:1-11..

2.?Hu X, et al. Phase 1 dose-escalation study to evaluate the safety, tolerability, pharmacokinetics, and anti-tumor activity of?FCN-159?in adults with neurofibromatosis type 1-related unresectable plexiform neurofibromas. BMC Med. 2023 Jul 3;21(1):230. doi: 10.1186/s12916-023-02927-2.



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